October is Rett Syndrome Awareness Month. Rett Syndrome is a complex neurological disorder that mainly affects girls in a variety of racial and ethnic groups worldwide. Rett syndrome (RS) is often ...
Patients and families facing a Rett syndrome diagnosis experience an array of burdens. Paige Nues: The treatment burden of Rett syndrome is complex. It’s one of the most pervasive, severe neurologic ...
Neurogene Gene Therapy Shows Signs of Efficacy in Small Study, But an Adverse Event Spooks Investors
A Neurogene gene therapy in development for the rare neurodevelopmental disorder Rett syndrome has encouraging early data in a small group of patients, an interim readout that comes a week after a ...
Individuals with RS require a variety of therapies throughout their lives. [49] These include physical and occupational therapies to promote sitting, standing, ambulation and fine motor functions.
New preclinical data at ESGCT Congress highlight NGN-401 best-in-class potential and add to body of evidence that ICV administration is superior to IT-L in reaching key brain regions underlying Rett ...
Taysha Gene Therapies (TSHA) has made great progress recently in advancing its gene therapy known as TSHA-102 for the treatment of patients with Rett Syndrome. Despite only having data from one ...
Occupational therapy (OT) helps you regain your ability to perform daily tasks and live independently. OTs create personalized plans to help improve your physical, emotional, and social needs. An OT ...
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