Scientists investigating the severe developmental disorder known as Rett syndrome have discovered a series of crucial molecular changes that occur long before symptoms appear. The findings could be ...

The My Rett Ally web app, powered by mejo, is a new resource to support caregivers of individuals with Rett syndrome. My Rett Ally, a web application powered by mejo, is specifically designed for Rett ...

Real World Data from LOTUS Study Evaluating Long-term Efficacy and Tolerability Outcomes of DAYBUE® (trofinetide) in Patients with Rett Syndrome Published in Developmental Medicine and Child Neurology ...

New discoveries about the severe developmental disorder known as Rett syndrome could open the door to better treatments for the devastating, life-shortening condition. Scientists investigating the ...

SAN DIEGO--(BUSINESS WIRE)--Acadia Pharmaceuticals Inc. (Nasdaq: ACAD) today announced that Health Canada has granted marketing authorization of DAYBUE™ (trofinetide) for the treatment of Rett ...

UAB will study a drug originally developed for Parkinson’s disease that may help reduce breath holding in patients with Rett syndrome. Pediatric neurologist Alan Percy, M.D., is a leading clinician ...

Dominique Pichard, M.D., returns as Chief Science Officer, and Staci Almager joins as Chief Development Officer. As the mother of an individual with Rett, I'm honored to rejoin this community at such ...

Taysha Gene Therapies has unfurled more data in the developmental disorder Rett syndrome, linking its gene therapy to improvements in the first adults and children to receive low doses of the ...

A new article published in the Cell Reports describes how a new drug is able to reduce the symptoms and activate the dormant neurons characteristic of Rett syndrome in preclinical models. The study ...

On an unseasonably warm day in late February, scientists at Kunming Medical University’s Experimental Animal Center in the far southwestern province of Yunnan injected a female crab-eating macaque ...